Active Clinical Trials

Clinical trials are at the heart of our work to bring innovative medicines to people with a particular disease or condition. Learn more about the active studies conducted by Novartis including opportunities to get involved.

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Study title Condition Phase Location

Effectiveness and Safety of Tisagenlecleucel Therapy in Brazilian Patients With B-lymphocyte Malignancies

Diffuse Large B-cell Lymphoma, Acute Lymphoblastic Leukemia, Follicular Lymphoma Brazil

A Study of Efficacy and Safety of Ianalumab Versus Placebo in Addition to Eltrombopag in Primary Immune Thrombocytopenia Patients Who Failed Steroids

Primary Immune Thrombocytopenia Phase3 Argentina
Australia
Austria
Belgium
China
Czechia
France
Germany
Hungary
India
Italy
Japan
Korea, Republic of
Malaysia
Mexico
Netherlands
Norway
Philippines
Romania
Singapore
Spain
Taiwan
Thailand
Turkey
United Kingdom
United States
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Adjuvant Dabrafenib and Trametinib Treatment in Patients With Completely Resected High-risk Stage III Melanoma.

Melanoma Turkey

NEPC Study: An Exploratory Safety and Efficacy Study With PSMA, SSTR2 and GRPR Targeted Radioligand Therapy in Metastatic Neuroendocrine Prostate Cancer.

Metastatic Neuroendocrine Prostate Cancer Phase1 France
Spain
United States

Concentration of Ofatumumab in the Breast Milk of Lactating Women With Relapsing Forms of Multiple Sclerosis

Multiple Sclerosis Phase4 Germany
United Kingdom
United States

Long-term Safety and Tolerability of Iptacopan in Patients With Paroxysmal Nocturnal Hemoglobinuria

Paroxysmal Nocturnal Hemoglobinuria Phase3 France
Germany
Italy
Spain
United Kingdom
United States
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The Gilenya Pregnancy Registry

Multiple Sclerosis Argentina
Australia
Austria
Belgium
Brazil
Canada
Colombia
Cyprus
Czechia
Denmark
Finland
France
Germany
Greece
Hungary
Ireland
Israel
Italy
Lebanon
Mexico
Netherlands
Poland
Portugal
Romania
Russian Federation
Saudi Arabia
Slovakia
Slovenia
Spain
Sweden
Switzerland
United Arab Emirates
United Kingdom
United States
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Study Assessing the Efficacy, Safety and PK of Alpelisib (BYL719) in Pediatric and Adult Patients With PIK3CA-related Overgrowth Spectrum

PIK3CA-related Overgrowth Spectrum (PROS) Phase2 Canada
France
Germany
Italy
Netherlands
Spain
Switzerland
United Kingdom
United States
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First in Human Study to Assess the Safety, Tolerability and Pharmacokinetics of EDI048 in Healthy Volunteers

Healthy Volunteers Phase1 United Kingdom

An Open-label Study Comparing Lutetium (177Lu) Vipivotide Tetraxetan Versus Observation in PSMA Positive OMPC.

Oligometastatic Prostate Cancer (OMPC) Phase3 Australia
Austria
Belgium
Canada
Czechia
France
Hungary
Israel
Italy
Japan
Singapore
Slovakia
Spain
Switzerland
Taiwan
United States
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