
Tags Archive Navigation
icon
-
Addressing unmet needs for inherited neuromuscular diseases
-
Novartis announces partnership with the American Society of Hematology to fight sickle cell disease in Sub-Saharan Africa
-
Breaking down barriers for patients with sickle cell disease
-
Discovery gives cystic fibrosis researchers new direction
-
When tiny brains are best for brain research
-
Fixing what’s lost in translation
-
Eye disease tracked to a glitch in starburst cells
-
Electrical brainstorms traced to genetic mutations
-
Small viruses could accelerate cell and gene therapy research
-
Rewriting the playbook for clinical testing in a rare disease
-
Rare speed on a rare disease
-
Novartis researches SMA’s genetic roots